Amicus Therapeutics
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Amicus Therapeutics

http://www.amicustherapeutics.com/
Last activity: 16.01.2026
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Categories: BioTechGeneticsPharmaceuticalRareDiseaseTherapeutics
We are a global, patient-dedicated biotechnology company focused on discovering, developing, and delivering high-quality medicines for people living with rare metabolic diseases.

Amicus is the Latin word for friend. This name signifies our collaborative approach to developing medicines by incorporating the patient perspective every step of the way. Our company was founded by an entrepreneur who embarked on a life-long journey to transform the lives of those living with devastating conditions when two of his children were diagnosed with a rare disease. That spirit of empathy, compassion, and tenacity permeates our culture and influences all aspects of our approach to advancing cutting-edge technologies.

With one rare disease medicine globally commercialized for Fabry disease, an investigational enzyme replacement therapy in late stage development for the treatment of Pompe disease, and a robust gene therapy pipeline and growth platform for lysosomal storage disorders, we are committed to changing the lives of people with these life-threatening conditions.

Building on our core beliefs, our mission-focused behaviors help us define and shape our culture; drive performance and innovation; inform development and growth; and attract, energize, and retain the right talent. By championing mission-dedication, innovation, performance, and integrity, we are united by our passion for making a difference and committed to pushing ideas as far and as fast as possible.

Our global footprint spans over 20 countries, including our global headquarters in Philadelphia, PA and international headquarters in Marlow, UK. Additional international office locations include Australia, Canada, France, Japan, Germany, Italy, The Netherlands, and Spain. More information about Amicus and our career opportunities can be found at www.amicusrx.com.
Mentions
14
Location: United States
Total raised: $92M
Founded date: 2002

Investors 1

DateNameWebsite
07.08.2021New Enterp...nea.com

Funding Rounds 1

DateSeriesAmountInvestors
18.05.2007IPO$92M-

Mentions in press and media 14

DateTitleDescription
16.01.2026Making U.S. biotech more competitive with China’s could help rare disease patients, experts sayTo share your story, or find out how to get involved with CNBC Cures, email CNBC.cures@cnbc.com China is pumping money into its biotech industry, helping launch a new wave of labs and incubators in the country. Experts say this could slow d...
15.12.2025DMX-200 ACTION3 PHASE 3 TRIAL COMPLETES RECRUITMENTRecruitment successfully completed in Dimerix' ACTION3 Phase 3 clinical trial[1], which has recruited and dosed its target 286th adult patient The ACTION3 Phase 3 trial explores the efficacy and safety of DMX-200 in FSGS patients when dosed...
22.08.2024Global Genes' Annual Week in RARE Event Heading to Kansas CityGlobal Genes Global Genes is taking Week In RARE on the road to Kansas City, after having hosted this annual event in California for over 12 years. Moving the location annually will help make the event more accessible and equitable to the g...
12.07.2012Biotech with Lysosomal storage disorder treatment raising $3.5 million, doubles staffHung Do, the chief science officer of Callidus Biopharma, based at the Pennsylvania Biotechnology Center in Doylestown, Pennsylvania, told MedCity News that he believes the enzyme replacement therapies currently on the market are inefficien...
16.04.2012Amicus Therapeutics names new CFOCurrently, Genzyme is the only other company that provides a drug for this disease since Shire dropped its efforts to get the drug approved after years of back-and-forth with the U.S. Food and Drug Administration. The Cranbury, New Jersey-b...
20.01.2012Lysosomal storage disorder treatment moving into proof-of-concept phaseDo said although a handful of FDA-approved protein therapies, enzyme replacement therapies (ERTs) were developed to treat lysosomal storage diseases, the ERTs are not “optimal.” He explained that the current therapies each have deficiencies...
11.10.2011Azelon secures $4.5 million in Series A funding, restructures companyThe financing has prompted a restructuring of the company, formerly called Zelos Therapeutics. Don Hayden has been appointed executive chairman and Joan Lau has been named president and CEO. Lau succeeds Brian MacDonald, who will remain wit...
26.07.2007Biotech financing: Will ImaRx break the IPO slump?(UPDATED: See below.) It’s been a long, barren summer for biotech IPOs, but ImaRx, the blood-clot company we featured here, finally managed to bull its way into the public markets. The company, which withdrew an earlier $75 million IPO and ...
31.05.2007Amicus Therapeutics prices IPO, raising up to $86MCranbury, N.J.-based Amicus Therapeutics priced its IPO shares at $15, right in the middle of its expected $14 to $16 range, an offering that could raise up to $86.3 million in gross proceeds if it sells all 5.75 million shares available. H...
18.05.2007Amicus Therapeutics aims for potentially disruptive $92M IPOAmicus Therapeutics, a Cranbury, N.J., developer of drugs to treat rare genetic diseases, said it plans to raise as much as $92 million in an IPO — money that would fund its pursuit of new drugs for rare genetic diseases, a strategy could b...
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